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SRPK2 and Congenital Heart Disease

Exome sequencing in a three‑generation family with atrial septal defects identified a candidate variant in SRPK2 (HGNC:11306) for congenital heart disease (MONDO_0005453). Specifically, the c.2044C>T (p.Pro682Ser) variant was detected in 2 affected probands (PMID:27989580), and segregation analyses indicated co‑segregation with the disease phenotype. However, previous functional studies did not reveal significant alteration of protein signaling, thereby reducing confidence in the variant’s pathogenic role.

Although the genetic data from this familial case supports a possible contribution of SRPK2 to congenital heart disease, the conflicting functional evidence leaves the association in doubt. Consequently, the overall gene‑disease association is classified as disputed. Additional independent studies are required to resolve these discrepancies and to clarify the clinical utility of incorporating SRPK2 genetic findings into diagnostic decision‑making.

References

  • International journal of cardiology • 2017 • The promises and challenges of exome sequencing in familial, non‑syndromic congenital heart disease PMID:27989580

Evidence Based Scoring (AI generated)

Gene–Disease Association

Disputed

Evidence from a three‑generation family with 2 affected probands (PMID:27989580) showed co‑segregation of the SRPK2 c.2044C>T (p.Pro682Ser) variant with congenital heart disease; however, prior functional studies significantly weaken its candidacy.

Genetic Evidence

Limited

The genetic evidence is restricted to a single family with 2 affected individuals, and the variant has not been recurrently reported in independent cohorts (PMID:27989580).

Functional Evidence

Limited

Functional assays demonstrated minimal impact on protein signaling, which does not support a robust pathogenic mechanism for SRPK2 in congenital heart disease (PMID:27989580).