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Congenital methemoglobinemia due to HBB-encoded hemoglobin M variants is characterized by life-long cyanosis and elevated methemoglobin levels. Heterozygous substitutions act via a dominant-negative effect to destabilize the heme environment and accelerate autooxidation to methemoglobin. The beta28(B10)Leu→Met variant (c.85C>A (p.Leu29Met)) was identified in a multi-generation Chilean family with chronic methemoglobinemia and unstable hemoglobin (PMID:10335980). Separately, the beta92(His93)His→Tyr substitution (c.277C>T (p.His93Tyr)) was found in an unrelated patient with congenital methemoglobinemia and Hb E trait (PMID:9494043). Functional assays confirm increased methemoglobin formation consistent with this phenotype ([PMID:10335980]).
Gene–Disease AssociationLimitedTwo unrelated probands ([PMID:10335980], [PMID:9494043]), segregation in one family (3 affected relatives [PMID:10335980]), concordant functional data Genetic EvidenceLimitedTwo heterozygous HBB variants in separate probands with hemoglobin M disease and minimal segregation Functional EvidenceModerateFunctional assays demonstrate unstable hemoglobin variants with increased methemoglobin formation consistent with clinical phenotype |